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Vertex Pharmaceuticals
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Vertex Casgevy wins landmark FDA approval for toddlers with SCD and TDT
The expanded label is expected to make about 5,500 additional children in the United States eligible for treatment.
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Abu Dhabi’s Yas Clinic successfully delivers landmark CASGEVY gene treatment
This cutting-edge approach represents a major advancement in how doctors can treat genetic diseases by directly modifying the faulty genes responsible for these conditions.